Tuesday, May 10, 2022

Gene therapy could treat Pitt-Hopkins syndrome, proof-of-concept study suggests

Scientists reported on an experimental gene-therapy-like technique to restore the normal activity of the TCCF4 gene deficient in individuals with Pitt-Hopkins syndrome.

from Top Health News -- ScienceDaily https://ift.tt/9ufGPOi

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Scientists discover an “impossible” cellular survival pathway that could help fight cancer

Scientists discovered a surprising backup system that lets mammalian cells make the essential amino acid cysteine even when the pathways onc...